RT Book, Section
A1 Douglas, Vanja C.
A1 Aminoff, Michael J.
A2 Papadakis, Maxine A.
A2 McPhee, Stephen J.
A2 Rabow, Michael W.
A2 McQuaid, Kenneth R.
SR Print(0)
ID 1193129679
T1 Myopathic Disorders
T2 Current Medical Diagnosis & Treatment 2023
YR 2023
FD 2023
PB McGraw-Hill Education
PP New York, NY
SN 9781264687343
LK accessmedicine.mhmedical.com/content.aspx?aid=1193129679
RD 2024/04/18
AB Key  Clinical  Updates  in  Myopathic  DisordersCasimersen  is  FDA-approved  for  treatment  of  Duchenne  muscular  dystrophy;  it  shows  benefit  in  patients  with  a  mutation  amenable  to  exon  45  skipping.